Topics:
Neurology • Neuromuscular
In patients with Duchenne Muscular Dystrophy who have an exon 51 mutation, do you treat with both prednisone and Eteplirsen?
What are common side effects to look out for with Eteplirsen?
Answer from: at Community Practice
From our very first patient treated in clinical trial with our partner Sarepta, we continued pre-treatment with corticosteroids. This was true for all subjects in the first trial that was published (Mendell et al., PMID 23907995). This led to FDA approval for Eteplirsen (EXONDYS 51).Corticosteroid t...
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