How do you approach symptomatic thalassemia intermedia patients from beta thal trait with alpha gene duplication?
How do you approach whether to start transfusions, and would you consider HU, mitapivat, or luspatercept?
1 Answer
Mednet MemberInvited Expert
Pediatric Hematology/Oncology · Weill Cornell Medical College
Answered on · Updated on
Individuals with the beta-thalassemia trait and alpha-globin gene duplication have an intermediate phenotype. The severity depends on the type of beta mutation and whether the duplication is of alpha-1 or alpha-2, since these determine the imbalance between alpha and beta globin production. Individu...
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